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Mucopolysccharidosis VII Disease Monitoring Program (MPS VII DMP)
MPSVII_DMP
What is the goal of the study?
The aim of this study is to collect data on patients with MPS VII to provide a comprehensive dataset on the clinical presentation, heterogeneity, and disease progression, as well as meaningful standardized ICH GCP-quality data collected in-clinic across multiple sites globally.
Who can participate in the study?
Everyone