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Clinical Trial Search block Test

Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program (LC-FAOD DMP)

UX007-CL401

Phase: Post-Approval/Marketing
Clinicaltrials.gov ID: NCT04632953

What is the goal of the study?

The purpose of this study is to investigate the long-term safety and effectiveness of triheptanoin in adults and pediatric patients with LC-FAOD and to assess pregnancy and maternal complications in all patients with LC-FAOD, and adverse effects on the developing fetus, neonate, and infant.

Who can participate in the study?

Everyone

Study Team:

PI (Study Doctor): Terry Kho
Study Team Member: Hayden Vreugdenhil, hayden.vreugdenhil@seattlechildrens.org