Search Results

ARAR2221: A Phase 2 Study Using Chemoimmunotherapy with Gemcitabine, Cisplatin and Nivolumab in Newly Diagnosed Nasopharyngeal Carcinoma (NPC)-STUDY00004959

Nasopharyngeal carcinoma (NPC) is a tumor of epidermoid origin with unique histologic, epidemiologic and biological characteristics. In its...

Endoscopic versus Shunt Treatment of Hydrocephalus in Infants-STUDY00002138

Hydrocephalus is a neurological condition that primarily affects infants under one year of age. Shunt placement and Endoscopic Third...

Cranial Base Registry-STUDY00001830

The objective of the study is to establish a prospective registry of skull/cranial base patients in order to improve management, particularly...

Defining the Genetic Etiology of Suppurative Lung Disease in Children and Adults (GDMCC 5906)-STUDY00002760

We have established a Consortium of 8 geographically-dispersed clinical research sites in North America that are designed to study rare diseases...

Home Pulmonary Rehabilitation for Children with Early Onset Scoliosis-STUDY00004949

The goal of this project is to improve quality of life and pulmonary outcomes in children with severe early onset scoliosis (EOS) with an at-home...

Expanded Access To Provide Pegzilarginase To Patients with Arginase 1 Deficiency on Individual INDs with Pegzilarginase-STUDY00004901

For patients deficient in arginase 1 there is a significant unmet need for a therapy that will lower arginine levels to within the normal range...

Executive function in children with sleep disorders-STUDY00003188

To learn more about this study, please email the study team member listed below.

PNEUMOCOCCAL TITERS IN PATIENTS TREATED WITH B CELL-DIRECTED CHIMERIC ANTIGEN RECEPTOR EXPRESSING T CELLS-STUDY00003630

This research aims to determine whether a dose of pneumococcal vaccine prior to B cell directed CART therapy will boost pneumococcal immunity and...

EPITOPE OPEN-LABEL EXTENSION STUDY TO EVALUATE THE LONG-TERM CLINICAL BENEFIT AND SAFETY OF DBV712 IN PEANUT-ALLERGIC CHILDREN (EPOPEX)-STUDY00002112

To learn more about this study, please email the study team member listed below.

Phase 2 Randomized, Double-blind, Placebocontrolled, Study of Zatolmilast (BPN14770) in Subjects with PPP2R5D Neurodevelopmental Disorder (Jordan's Syndrome)-STUDY00005037

This is a multi-center, Phase 2, randomized, double-blind, placebo-controlled, study with an open label extension to obtain preliminary assessment...